Externally-Led Patient-Focused Drug Development Meeting for ARPKD
Agenda
*all times in CST
1:00-1:05 p.m. | Opening Remarks | Matt Becka – PKDF |
1:05-1:20 p.m. | Recap of EL-PFDD: What’s Important to ARPKD Patients/Caregivers | Larry Bauer – Hyman, Phelps & McNamara |
1:20-1:30 p.m. | Framework for Integrating the Patient Voice into Drug Development | James Valentine – Hyman, Phelps & McNamara |
1:30-1:40 p.m. | Opportunities to Conduct Clinical Trials in ARPKD | Lisa Guay-Woodford – CHOP |
1:40-2:15 p.m. | Panel Discussion: Perspectives on Facilitating Clinical Trials in ARPKD | |
2:15-2:25 p.m. | Landscape Analysis of Tools to Evaluate What’s Important to ARPKD Patients | Katherine Dell – Cleveland Children’s |
2:25-2:55 p.m. | Panel Discussion: Setting a Patient-Focused Research Agenda for Drug Development Tools | |
2:55-3:00 p.m. | Closing Remarks | Matt Becka – PKDF |
Panelists:
– Lisa Guay-Woodford, CHOP
– Katherine Dell, Cleveland Children’s
– Erum Hartung, CHOP
– Max Liebau, University of Cologne
– Djalila Mekahli, KU Leuven
Meeting organizers
Meeting sponsors